[Progressive convulsive encephalopathy: considering a abnormality of biopterin metabolism]

Arch Pediatr. 1999 Jul;6(7):759-61. doi: 10.1016/s0929-693x(99)80360-1.
[Article in French]

Abstract

Background: Symptomatic forms of hyperphenylalaninemia are rare in France since neonatal screening began.

Case report: A child born in Algeria from consanguinous parents was referred at 2 years of age for a severe epileptic encephalopathy with hypotonia. Amino acid chromatography revealed hyperphenylalaninemia due to a dihydropteridine reductase deficiency. Dietary restriction of phenylalanine and oral administration of amine precursors, L-dopa and 5-hydroxytryptophan had poor efficiency on epilepsy and psychomotor delay.

Conclusion: Diagnosis of hyperphenylalaninemia must be evoked in any children with progressive encephalopathy born in country where neonatal screening is not performed.

Publication types

  • Case Reports
  • English Abstract

MeSH terms

  • 5-Hydroxytryptophan / therapeutic use
  • Algeria / ethnology
  • Anticonvulsants / therapeutic use
  • Biopterins / blood
  • Biopterins / metabolism*
  • Biopterins / urine
  • Brain / pathology
  • Child, Preschool
  • Consanguinity
  • Developmental Disabilities / drug therapy
  • Developmental Disabilities / etiology*
  • Diet Therapy
  • Epilepsy / diagnosis
  • Epilepsy / drug therapy
  • Epilepsy / etiology*
  • France
  • Humans
  • Levodopa / therapeutic use
  • Magnetic Resonance Imaging
  • Male
  • Neopterin / blood
  • Phenylalanine / blood*
  • Phenylketonurias*

Substances

  • Anticonvulsants
  • Biopterins
  • Levodopa
  • Phenylalanine
  • Neopterin
  • 5-Hydroxytryptophan