Efficient lentiviral transduction of liver requires cell cycling in vivo

Nat Genet. 2000 Jan;24(1):49-52. doi: 10.1038/71673.

Abstract

Human-immunodeficiency-virus (HIV)-based lentiviral vectors are a promising tool for in vivo gene therapy. Unlike Moloney-murine-leukaemia-based retroviruses (MLV), lentiviruses are believed to stably transduce quiescent (non-cycling) cells in various organs. No previous studies, however, have directly established the cell-cycle status of any transduced cell type at the time of vector administration in vivo. In vitro studies using wild-type HIV or HIV-based vectors have shown that, in some cases, cell-cycle activation is required for infection, even though cellular mitosis is not an absolute requirement for integration. Even if the block in reverse transcription is overcome in quiescent T cells, productive infection by HIV cannot be rescued in the absence of cell-cycle activation. The potential use of these vectors for gene therapy prompted our study, which establishes a cell-cycle requirement for efficient transduction of hepatocytes in vivo.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cell Cycle / genetics*
  • Cell Line
  • Female
  • Genetic Vectors
  • Humans
  • Lentivirus / genetics*
  • Liver / cytology
  • Liver / enzymology
  • Liver / metabolism*
  • Mice
  • Mice, Inbred C57BL
  • Mice, SCID
  • Rats
  • Rats, Inbred F344
  • Transduction, Genetic*