Structure-based design of potent, amidine-derived inhibitors of factor Xa: evaluation of selectivity, anticoagulant activity, and antithrombotic activity

J Med Chem. 2000 Mar 9;43(5):883-99. doi: 10.1021/jm9903287.

Abstract

To enhance the potency of 1,2-dibenzamidobenzene-derived inhibitors of factor Xa (fXa), an amidine substituent was incorporated on one of the benzoyl side chains to interact with Asp189 in the S1 specificity pocket. Lead molecule 1 was docked into the active site of fXa to facilitate inhibitor design. Subsequently, iterative SAR studies and molecular modeling led to a 1000-fold increase in fXa affinity and a refined model of the new inhibitors in the fXa active site. Strong support for the computational model was achieved through the acquisition of an X-ray crystal structure using thrombin as a surrogate protein. The amidines in this series show high levels of selectivity for the inhibition of fXa relative to other trypsin-like serine proteases. Furthermore, the fXa affinity of compounds in this series (K(ass) = 50-500 x 10(6) L/mol) translates effectively into both anticoagulant activity in vitro and antithrombotic activity in vivo.

MeSH terms

  • Amidines / chemical synthesis*
  • Amidines / chemistry
  • Amidines / metabolism
  • Amidines / pharmacology
  • Animals
  • Anticoagulants / chemical synthesis*
  • Anticoagulants / chemistry
  • Anticoagulants / metabolism
  • Anticoagulants / pharmacology
  • Binding Sites
  • Crystallography, X-Ray
  • Dogs
  • Drug Design
  • Enzyme Inhibitors / chemical synthesis*
  • Enzyme Inhibitors / chemistry
  • Enzyme Inhibitors / metabolism
  • Enzyme Inhibitors / pharmacology
  • Factor Xa / chemistry
  • Factor Xa / metabolism
  • Factor Xa Inhibitors*
  • Fibrinolytic Agents / chemical synthesis*
  • Fibrinolytic Agents / chemistry
  • Fibrinolytic Agents / metabolism
  • Fibrinolytic Agents / pharmacology
  • Humans
  • In Vitro Techniques
  • Male
  • Models, Molecular
  • Prothrombin Time
  • Rabbits
  • Rats
  • Rats, Sprague-Dawley
  • Structure-Activity Relationship
  • Thrombin / chemistry
  • Thrombin / metabolism
  • Thrombosis / drug therapy

Substances

  • Amidines
  • Anticoagulants
  • Enzyme Inhibitors
  • Factor Xa Inhibitors
  • Fibrinolytic Agents
  • Thrombin
  • Factor Xa