Familial mitochondrial intestinal pseudo-obstruction and neurogenic bladder

J Child Neurol. 2000 Jun;15(6):386-9. doi: 10.1177/088307380001500606.

Abstract

Intestinal dysmotility and neurogenic bladder have been described as part of two autosomal-recessive mitochondrial disorders assumed to be due to a defect in communication between the nuclear and mitochondrial genomes: myoneurogastrointestinal encephalopathy (MNGIE) and diabetes insipidus, diabetes mellitus, optic atrophy, and deafness (Wolfram syndrome). Partial cytochrome c oxidase deficiency has been described in both. We describe three Ashkenazi Jewish siblings with progressive intestinal dysmotility, neurogenic bladder, and autonomic manifestations but no central nervous system involvement. Cytochrome c oxidase deficiency was demonstrated in peripheral and multiple intestinal muscle biopsies. Mitochondrial DNA analysis of an intestinal biopsy of patient 1 showed heteroplasmy consisting of a normal 16.5-kb band and an approximately 28-kb band, suggestive of a duplication. Mitochondrial DNA analysis of a muscle biopsy of patient 2 showed multiple deletions, mainly 10- and 11-kb bands. We suggest that this unique combination of intestinal pseudo-obstruction and neurogenic bladder could comprise a new autosomal-recessive mitochondrial disorder.

Publication types

  • Case Reports

MeSH terms

  • Adolescent
  • Adult
  • Autonomic Nervous System Diseases / etiology
  • Child
  • Cytochrome-c Oxidase Deficiency*
  • DNA Mutational Analysis
  • DNA, Mitochondrial / genetics
  • Electron Transport Complex IV / genetics
  • Female
  • Genetic Predisposition to Disease
  • Humans
  • Intestinal Pseudo-Obstruction / enzymology
  • Intestinal Pseudo-Obstruction / etiology*
  • Jews / genetics
  • Male
  • Mitochondrial Myopathies / complications
  • Mitochondrial Myopathies / enzymology
  • Mitochondrial Myopathies / genetics*
  • Muscle, Smooth / pathology
  • Syndrome
  • Urinary Bladder, Neurogenic / enzymology
  • Urinary Bladder, Neurogenic / etiology*

Substances

  • DNA, Mitochondrial
  • Electron Transport Complex IV