Efficient adenoviral vector transduction of human hematopoietic SCID-repopulating and long-term culture-initiating cells

Hum Gene Ther. 2000 Jun 10;11(9):1313-27. doi: 10.1089/10430340050032410.

Abstract

This article presents our studies on the adenoviral transduction efficiency, level of transgene expression, cell cycle status, and multilineage reconstitution ability of human CD34+ hematopoietic cells transduced under proliferating and survival growth conditions. Bone marrow and umbilical cord blood CD34+ cells were cultured in serum-free medium under survival conditions with thrombopoietin (Tpo) alone, or under proliferating conditions with Tpo, c-Kit ligand (KL), and Flt3 ligand (FL). Adenoviral vectors carrying the enhanced green fluorescent protein (EGFP) gene under the control of the PGK-1 promoter were used to transduce CD34+ cells. Approximately 10% of CD34+ cells were EGFP+ under both culture conditions. In contrast, up to 50% of CD34+CD38- cells were EGFP+, whereas a maximum of 8% of CD34+CD38(high) cells were EGFP+ (p < 0.001). Both colony-forming unit cells (CFU-C) and 5-week long-term culture-initiating cells (LTC-ICs) were efficiently transduced. Under survival conditions, a substantial fraction of transduced CD34+ cells remained quiescent. The nondividing CD34+EGFP+ cells contained LTC-ICs capable of reconstituting longterm culture for as long as 10 weeks. CD34+EGFP+ cells also retained the ability to engraft and multilineage-reconstitute NOD/SCID mice. These observations demonstrate that primitive human hematopoietic progenitor cells can be efficiently transduced by adenoviral vectors.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • ADP-ribosyl Cyclase
  • ADP-ribosyl Cyclase 1
  • Adenoviridae
  • Animals
  • Antigens, CD*
  • Antigens, CD34 / analysis
  • Antigens, Differentiation / analysis
  • Bone Marrow Cells / cytology
  • Cell Division
  • Cell Lineage
  • Cell Survival
  • Fetal Blood / cytology
  • Gene Expression
  • Genetic Vectors / genetics*
  • Green Fluorescent Proteins
  • Hematopoietic Stem Cell Transplantation*
  • Hematopoietic Stem Cells / metabolism
  • Humans
  • Luminescent Proteins / genetics
  • Membrane Glycoproteins
  • Membrane Proteins / physiology
  • Mice
  • Mice, SCID
  • NAD+ Nucleosidase / analysis
  • Stem Cell Factor / physiology
  • Thrombopoietin / physiology
  • Transduction, Genetic*

Substances

  • Antigens, CD
  • Antigens, CD34
  • Antigens, Differentiation
  • Luminescent Proteins
  • Membrane Glycoproteins
  • Membrane Proteins
  • Stem Cell Factor
  • flt3 ligand protein
  • Green Fluorescent Proteins
  • Thrombopoietin
  • ADP-ribosyl Cyclase
  • CD38 protein, human
  • Cd38 protein, mouse
  • NAD+ Nucleosidase
  • ADP-ribosyl Cyclase 1