Transduction of feline hematopoietic cells by oncoretroviral vectors pseudotyped with the subgroup A feline leukemia virus (FeLV-A)

Mol Ther. 2000 Jul;2(1):56-62. doi: 10.1006/mthe.2000.0090.

Abstract

The domestic cat is an outbred species with many identified analogues of human genetic diseases. Therefore, it has the potential to serve as a large animal model for evaluating the feasibility of hematopoietic stem cell gene therapy. This study compared gene transfer rates into feline hematopoietic progenitors by oncoretroviral vectors pseudotyped with the subgroup A feline leukemia virus (FeLV-A), the gibbon ape leukemia virus (GALV), and the murine amphotropic virus. Gene transfer rates were superior with the FeLV-A pseudotypes, which were then tested for their ability to transduce a cat hematopoietic repopulating cell. At more than 1 year posttransplantation, persistent marking was seen in both lymphoid and myeloid lineages of a myeloablated domestic cat that had received autologous marrow cells transduced with an FeLV-A pseudotyped vector.

Publication types

  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cats
  • Gene Transfer Techniques*
  • Genetic Vectors
  • Hematopoietic Stem Cells / metabolism*
  • Humans
  • Leukemia Virus, Feline / genetics*
  • Leukemia Virus, Gibbon Ape / genetics
  • Models, Genetic
  • Plasmids / metabolism
  • Polymerase Chain Reaction
  • Promoter Regions, Genetic
  • Retroviridae / genetics*
  • Time Factors
  • Transduction, Genetic*