Late-onset SCA2: 33 CAG repeats are sufficient to cause disease

Neurology. 2000 Aug 22;55(4):569-72. doi: 10.1212/wnl.55.4.569.

Abstract

SCA-2 is an autosomal dominant inherited disorder characterized by ataxia, slow saccades, and hyporeflexia. The authors evaluated a patient with a mild balance problem with a SCA-2 allele sized at 33 CAG repeats. The authors then ascertained her 91 year-old mother, who showed disease onset at age 86 with an SCA-2 allele of identical size. Their study indicates that 33 CAG repeats can be pathogenic at the SCA-2 locus, though such an allele may produce an extremely late onset and gradual rate of disease progression.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Aged
  • Aged, 80 and over
  • Alleles
  • Cerebellum / diagnostic imaging
  • Cerebellum / pathology
  • Disease Progression
  • Electrophoresis, Capillary
  • Female
  • Genes, Dominant
  • Humans
  • Magnetic Resonance Imaging
  • Male
  • Pedigree
  • Phenotype
  • Polymerase Chain Reaction
  • Spinocerebellar Ataxias / diagnosis*
  • Spinocerebellar Ataxias / etiology
  • Spinocerebellar Ataxias / genetics*
  • Tomography, X-Ray Computed
  • Trinucleotide Repeat Expansion / genetics*