Compound heterozygosity and nonsense mutations in the alpha(1)-subunit of the inhibitory glycine receptor in hyperekplexia

Hum Genet. 2001 Sep;109(3):267-70. doi: 10.1007/s004390100569.

Abstract

The alpha(1)-inhibitory glycine receptor is a ligand-gated chloride channel composed of three ligand-binding alpha1-subunits and two structural beta-subunits that are clustered on the postsynaptic membrane of inhibitory glycinergic neurons. Dominant and recessive mutations in GLRA1 subunits have been associated with a proportion of individuals and families with startle disease or hyperekplexia (MIM: 149400). Following SSCP and bi-directional di-deoxy fingerprinting mutational analysis of 22 unrelated individuals with hyperekplexia and hyperekplexia-related conditions, we report further novel missense mutations and the first nonsense point mutations in GLRA1, the majority of which localise outside the regions previously associated with dominant, disease-segregating mutations. Population studies reveal the unique association of each mutation with disease, and reveals that a proportion of sporadic hyperekplexia is accounted for by the homozygous inheritance of recessive GLRA1 mutations or as part of a compound heterozygote.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Sequence
  • Base Sequence
  • Codon, Nonsense
  • DNA Fingerprinting
  • DNA, Complementary / genetics
  • Heterozygote
  • Humans
  • Muscle Hypertonia / genetics*
  • Mutation, Missense
  • Polymorphism, Single-Stranded Conformational
  • Receptors, Glycine / genetics*
  • Reflex, Abnormal / genetics*
  • Reflex, Startle / genetics*

Substances

  • Codon, Nonsense
  • DNA, Complementary
  • GLRA1 protein, human
  • Receptors, Glycine

Associated data

  • OMIM/149400