Lentiviral gene transfer into peripheral blood-derived CD34+ NOD/SCID-repopulating cells

Blood. 2002 Jan 15;99(2):709-12. doi: 10.1182/blood.v99.2.709.

Abstract

This study reports a lentiviral gene transfer protocol for efficient transduction of adult human peripheral blood (PB)-derived CD34+ NOD/SCID-repopulating cells (SRCs) using vesicular stomatitis virus-G protein (VSV-G)-pseudotyped lentiviruses encoding for enhanced green fluorescence protein (eGFP). Lentiviral stocks were concentrated by anion exchange chromatography, and transduction was performed under serum-free conditions at a multiplicity of infection (MOI) between 3 and 50. Similar transduction efficiencies were achieved in the presence and absence of cytokines. Transduction of PB-derived CD34+ cells at a MOI of 3 resulted in gene transfer efficiencies into SRCs of 9.2% and 12.0% in the absence and presence of cytokines, respectively. Using improved lentiviral vectors, transduction frequency varied between 42.0% (MOI 10) and 36.0% (MOI 50) with multilineage transgene expression within SRC-derived myeloid and lymphoid cells. The protocol described can be adapted for clinical application of lentiviral gene transfer into PB-derived CD34+ cells from adult patients.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Animals
  • Cell Line
  • Chromatography, Ion Exchange
  • Culture Media, Serum-Free
  • Cytokines / pharmacology
  • Genes, Reporter
  • Genetic Vectors / genetics*
  • Genetic Vectors / isolation & purification
  • Graft Survival
  • Green Fluorescent Proteins
  • Hematopoietic Stem Cell Transplantation*
  • Hematopoietic Stem Cells / metabolism
  • Hematopoietic Stem Cells / virology*
  • Humans
  • Lentivirus / genetics*
  • Lentivirus / isolation & purification
  • Luminescent Proteins / genetics
  • Membrane Glycoproteins*
  • Mice
  • Mice, Inbred NOD
  • Mice, SCID
  • Transfection
  • Vesicular stomatitis Indiana virus / physiology
  • Viral Envelope Proteins / physiology
  • Virus Assembly

Substances

  • Culture Media, Serum-Free
  • Cytokines
  • G protein, vesicular stomatitis virus
  • Luminescent Proteins
  • Membrane Glycoproteins
  • Viral Envelope Proteins
  • Green Fluorescent Proteins