CAG/CTG repeat expansions at the Huntington's disease-like 2 locus are rare in Huntington's disease patients

Neurology. 2002 Mar 26;58(6):965-7. doi: 10.1212/wnl.58.6.965.

Abstract

The authors report a large series of patients with Huntington disease (HD)-like phenotype without CAG repeat expansions in the IT15 gene that were screened for the newly identified CAG/CTG expansion in the gene encoding junctophilin-3. Normal alleles in controls had from 8 to 28 repeats. A single patient of North African origin with typical HD carried an allele with 50 uninterrupted repeats, representing approximately 2% of the non-IT15 HD patients tested. Therefore, further genetic heterogeneity is expected in HD.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Alleles
  • Brain / pathology
  • Child
  • Child, Preschool
  • Female
  • Humans
  • Huntington Disease / genetics*
  • Huntington Disease / pathology
  • Infant
  • Male
  • Membrane Proteins / genetics
  • Middle Aged
  • Trinucleotide Repeat Expansion / genetics*

Substances

  • Membrane Proteins
  • junctophilin