Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement

Nat Med. 2002 May;8(5):423-5. doi: 10.1038/nm0502-423.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Adenosine Deaminase / administration & dosage
  • Adenosine Deaminase / deficiency*
  • Adenosine Deaminase / genetics*
  • Adenosine Deaminase / metabolism
  • Adenosine Deaminase / therapeutic use*
  • Animals
  • Cattle
  • Genetic Therapy*
  • Humans
  • Lymphocyte Transfusion*
  • Severe Combined Immunodeficiency / therapy*
  • T-Lymphocytes / enzymology

Substances

  • Adenosine Deaminase
  • pegademase bovine