A recombinant CD7-specific single-chain immunotoxin is a potent inducer of apoptosis in acute leukemic T cells

Cancer Res. 2002 May 15;62(10):2848-55.

Abstract

A recombinant immunotoxin was constructed from the hybridoma antibody TH-69 directed against human CD7, a surface antigen of leukemic T cells. The antibody was subcloned as a single chain Fv (scFv) fragment and genetically linked to a truncated Pseudomonas exotoxin A fragment containing the catalytic domains II and III but lacking the receptor binding domain I. Domain I was replaced by the scFv, thus conferring restricted specificity for CD7-positive cells. The bacterially expressed and purified toxin retained binding specificity for CD7-positive cells. It promoted apoptosis in two CD7-positive cell lines derived from T-lineage acute lymphoblastic leukemias, CEM and Jurkat, but not in the CD7-negative B-lymphoid lines REH, Nalm-6, and SEM. Maximum killing in excess of 95% was reached after 96 h in CEM and Jurkat cells with a single dose of 100 ng/ml. Cells treated with a similarly constructed scFv-exotoxin A immunotoxin against melanoma-associated chondroitin sulfate proteoglycan, an antigen absent from leukemic T cells, remained unaffected. Lysis of target cells occurred via apoptosis as evidenced by staining with Annexin V and specific cleavage of poly(ADP-ribose) polymerase. Approximately 20% of leukemic cells from a patient with CD7-positive acute T-cell leukemia kept in long-term primary culture for 30 cell generations were killed within 96 h after treatment with the toxin. These findings justify further evaluation of the agent in view of potential therapeutic applications.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • ADP Ribose Transferases / pharmacology*
  • Animals
  • Antibody Specificity
  • Antigens, CD7 / immunology*
  • Apoptosis / drug effects*
  • Apoptosis / immunology
  • Bacterial Toxins*
  • COS Cells
  • Child
  • Epitopes / immunology
  • Exotoxins / pharmacology*
  • Female
  • Humans
  • Immunoglobulin Fragments / genetics
  • Immunoglobulin Fragments / immunology
  • Immunoglobulin Fragments / pharmacology
  • Immunotoxins / genetics
  • Immunotoxins / immunology
  • Immunotoxins / pharmacology*
  • Infant
  • Jurkat Cells / cytology
  • Jurkat Cells / drug effects
  • Leukemia, T-Cell / drug therapy*
  • Leukemia, T-Cell / immunology
  • Leukemia, T-Cell / pathology
  • Poly(ADP-ribose) Polymerases*
  • Protein Structure, Tertiary
  • Pseudomonas aeruginosa Exotoxin A
  • Recombinant Proteins / genetics
  • Recombinant Proteins / immunology
  • Recombinant Proteins / pharmacology
  • Tumor Cells, Cultured
  • Virulence Factors*

Substances

  • Antigens, CD7
  • Bacterial Toxins
  • Epitopes
  • Exotoxins
  • Immunoglobulin Fragments
  • Immunotoxins
  • Recombinant Proteins
  • Virulence Factors
  • ADP Ribose Transferases
  • Poly(ADP-ribose) Polymerases