Neuropathology of some hereditary conditions affecting central and peripheral nervous system

Acta Neurol Belg. 2002 Mar;102(1):30-5.

Abstract

Neuropathology plays a crucial role in the phenotypic individualization of hereditary disorders affecting the central and peripheral nervous system even if molecular genetics represents the most essential step in describing the genotypes. The neuropathological description of phenotypes and genotypes can be used for refining clinical skills and understanding many clinical, neurophysiological and neuroradiological features. It contributes to the diagnosis of such disorders. The use of immunohistochemical techniques in combination with molecular genetics improves also our knowledge of their pathogenesis and might participate to the future development of therapeutic strategies. We discuss new features of spino-cerebellar ataxia (SCA) type 7 and of a recently identified SCA17 in order to illustrate the significance of the neuronal intranuclear inclusions (NIIs) described in various CAG/polyglutamine repeat expansion diseases. In the field of the peripheral neuropathies we present data on a newly described autosomal recessive Charcot-Marie-Tooth disease (CMT4F) with mutations in the periaxin gene. We document a dysjunction between myelin loops and axolemma with disappearance of the septate-like junctions or transverse bands. The significance of this dysjunction is not yet elucidated. We hope to show by these examples that the combination of classical and new neuropathological methods is useful in the study of hereditary disorders of the nervous system.

Publication types

  • Review

MeSH terms

  • Central Nervous System / pathology*
  • Central Nervous System / physiopathology
  • Charcot-Marie-Tooth Disease / genetics
  • Charcot-Marie-Tooth Disease / pathology
  • Charcot-Marie-Tooth Disease / physiopathology
  • Heredodegenerative Disorders, Nervous System / pathology*
  • Heredodegenerative Disorders, Nervous System / physiopathology
  • Humans
  • Inclusion Bodies / genetics
  • Inclusion Bodies / metabolism
  • Inclusion Bodies / pathology
  • Membrane Proteins / genetics
  • Membrane Proteins / metabolism
  • Myelin Sheath / genetics
  • Myelin Sheath / metabolism
  • Myelin Sheath / pathology
  • Peripheral Nervous System / pathology*
  • Peripheral Nervous System / physiopathology
  • Spinocerebellar Ataxias / genetics
  • Spinocerebellar Ataxias / pathology
  • Spinocerebellar Ataxias / physiopathology

Substances

  • Membrane Proteins
  • periaxin