Autosomal recessive inheritance of RYR1 mutations in a congenital myopathy with cores

Neurology. 2002 Jul 23;59(2):284-7. doi: 10.1212/wnl.59.2.284.

Abstract

Central core disease (CCD) is a congenital myopathy due to dominant mutations in the skeletal muscle ryanodine receptor gene (RYR1). The authors report three patients from two consanguineous families with symptoms of a congenital myopathy, cores on muscle biopsy, and confirmed linkage to the RYR1 locus. Molecular genetic studies in one family identified a V4849I homozygous missense mutation in the RYR1 gene. This report suggests a congenital myopathy associated with recessive RYR1 mutations.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Biopsy
  • Child, Preschool
  • Consanguinity
  • Female
  • Homozygote
  • Humans
  • Muscle, Skeletal / pathology*
  • Muscular Diseases / congenital*
  • Muscular Diseases / genetics*
  • Muscular Diseases / pathology
  • Mutation, Missense*
  • Ryanodine Receptor Calcium Release Channel / genetics*

Substances

  • Ryanodine Receptor Calcium Release Channel