How does the threshold score to enter a major depression trial influence the size of the available patient population for study?

J Affect Disord. 2002 Sep;71(1-3):181-7. doi: 10.1016/s0165-0327(00)00369-4.

Abstract

Background: This paper describes the relationship between entry criteria and eligible population for inclusion in Major Depression (MD) clinical trials. Inclusion criteria for a MD study typically require patients to pass a threshold score on a depression rating scale, most commonly the HAM-D or MADRS. A Score To Enter (STE) of > or = 17 on the HAM-D 17-item scale is a typical value, although higher values (i.e. > or = 22 or even > or = 25 points) are often used. It is commonly supposed that patients with higher baseline scores form a more sensitive sample for discriminating active drug from placebo.

Method: We present data from a sample of depressed hospital outpatients and describe their general characteristics. We then introduce a model, based upon this sample, which predicts the impact of STE on eligible trial population.

Results and conclusion: A small increase in STE has a marked effect on eligible population: an increase in HAM-D (17 item) STE from 17 to 21 and 25 reduces the eligible population by 42 and 76%, respectively. These predictions are reasonably robust when our model is validated with known clinical trial data.

Clinical relevance: Our findings have major implications for planning and managing Major Depression trials as higher STEs substantially restrict the proportion of patient eligible for study.

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Clinical Trials as Topic*
  • Cohort Studies
  • Depressive Disorder / psychology*
  • Depressive Disorder / therapy*
  • Eligibility Determination*
  • Female
  • Humans
  • Male
  • Middle Aged
  • Psychiatric Status Rating Scales
  • Research Design
  • Sample Size*
  • Severity of Illness Index