Impaired trafficking of human kidney anion exchanger (kAE1) caused by hetero-oligomer formation with a truncated mutant associated with distal renal tubular acidosis

Biochem J. 2002 Dec 15;368(Pt 3):895-903. doi: 10.1042/BJ20020574.

Abstract

Autosomal dominant distal renal tubular acidosis (dRTA) has been associated with several mutations in the anion exchanger AE1 gene. The effect of an 11-amino-acid C-terminal dRTA truncation mutation (901 stop) on the expression of kidney AE1 (kAE1) and erythroid AE1 was examined in transiently transfected HEK-293 cells. Unlike the wild-type proteins, kAE1 901 stop and AE1 901 stop mutants exhibited impaired trafficking from the endoplasmic reticulum to the plasma membrane as determined by immunolocalization, cell-surface biotinylation, oligosaccharide processing and pulse-chase experiments. The 901 stop mutants were able to bind to an inhibitor affinity resin, suggesting that these mutant membrane proteins were not grossly misfolded. Co-expression of wild-type and mutant kAE1 or AE1 resulted in intracellular retention of the wild-type proteins in a pre-medial Golgi compartment. This dominant negative effect was due to hetero-oligomer formation of the mutant and wild-type proteins. Intracellular retention of kAE1 in the alpha-intercalated cells of the kidney would account for the impaired acid secretion into the urine characteristic of dRTA.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • 4-Acetamido-4'-isothiocyanatostilbene-2,2'-disulfonic Acid / pharmacology
  • Acidosis, Renal Tubular / genetics*
  • Acidosis, Renal Tubular / metabolism
  • Anion Exchange Protein 1, Erythrocyte / genetics*
  • Anion Exchange Protein 1, Erythrocyte / metabolism*
  • Biotinylation
  • Blotting, Western
  • Cell Line
  • Cell Membrane / metabolism
  • Endoplasmic Reticulum / metabolism
  • Genes, Dominant
  • Glycosylation
  • Humans
  • Immunohistochemistry
  • Kidney / metabolism
  • Mutation*
  • Oligosaccharides / chemistry
  • Plasmids / metabolism
  • Protein Structure, Tertiary
  • Time Factors
  • Transfection

Substances

  • Anion Exchange Protein 1, Erythrocyte
  • Oligosaccharides
  • SLC4A1 protein, human
  • 4-Acetamido-4'-isothiocyanatostilbene-2,2'-disulfonic Acid