Cytoskeletal derangements in hereditary myopathy with a desmin L345P mutation

Acta Neuropathol. 2002 Nov;104(5):493-504. doi: 10.1007/s00401-002-0583-z. Epub 2002 Jul 3.

Abstract

Patients with abnormal accumulations of desmin have been described in myopathies with or without cardiac involvement. Desmin deposits were sometimes associated with abnormal aggregates of other cytoskeletal proteins. In the present study we present how the cytoskeletal organisation of desmin, nestin, synemin, paranemin, plectin and alphaB-crystallin is altered in skeletal muscles from a patient with a L345P mutation in the desmin gene. In general, accumulations of desmin together with synemin, nestin, plectin and alphaB-crystallin were present between myofibrils and beneath the sarcolemma. However, as the biopsy samples were very myopathic, large variability in fibre size and fibre maturation was seen, thus the myofibrillar content and the cytoskeletal organisation varied considerably. In cultured satellite cells from the patient, desmin aggregates were not observed in initial passages, but occurred over time in culture in the form of perinuclear, peripheral or cytoplasmic deposits. Nestin colocalised to the abnormal desmin deposits to a larger extent than did vimentin. alphaB-Crystallin was only present in cells with a disrupted desmin network. Plectin was altered in a subset of cells with a disrupted desmin network, whereas synemin and paranemin were not detected. We conclude that the L345P desmin mutation has a profound influence on the cytoskeletal organisation both in vivo and in vitro, which reflects the pathogenesis of the desmin myopathy.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Cells, Cultured
  • Desmin / genetics
  • Desmin / metabolism*
  • Humans
  • Immunohistochemistry
  • Intermediate Filament Proteins / metabolism
  • Intermediate Filaments / metabolism*
  • Intermediate Filaments / pathology
  • Muscle Proteins / metabolism
  • Muscle, Skeletal / metabolism*
  • Muscle, Skeletal / pathology
  • Muscular Diseases / genetics
  • Muscular Diseases / metabolism*
  • Muscular Diseases / pathology*
  • Mutation
  • Nerve Tissue Proteins*
  • Nestin
  • Plectin
  • Satellite Cells, Skeletal Muscle / metabolism
  • Satellite Cells, Skeletal Muscle / pathology
  • alpha-Crystallin B Chain / metabolism

Substances

  • Desmin
  • Intermediate Filament Proteins
  • Muscle Proteins
  • NES protein, human
  • Nerve Tissue Proteins
  • Nestin
  • PLEC protein, human
  • Plectin
  • alpha-Crystallin B Chain
  • desmuslin