Non-myeloablative hematopoietic cell transplant for treatment of nonmalignant disorders in children

Int J Hematol. 2002 Aug:76 Suppl 2:271-7. doi: 10.1007/BF03165129.

Abstract

Hematopoietic stem cell transplantation (HCT) may offer the only curative therapy for certain life-threatening immune deficiency disorders. Conventional HCT poses a risk to patients for severe morbidity, mortality, and late sequelae resulting from myeloablative preparative regimens. This review summarizes the development of nonmyeloablative regimens that have the potential to reduce both short- and long-term risks of HCT. Results of NM-HCT in a small number of patients indicate that this procedure may play an important role in treatment of life-threatening immune deficiencies.

Publication types

  • Duplicate Publication
  • Research Support, U.S. Gov't, P.H.S.
  • Review

MeSH terms

  • Child
  • Graft vs Host Disease
  • Hematologic Diseases / therapy*
  • Hematopoietic Stem Cell Transplantation / adverse effects
  • Hematopoietic Stem Cell Transplantation / methods*
  • Humans
  • Immunologic Deficiency Syndromes / therapy
  • Immunosuppressive Agents / therapeutic use

Substances

  • Immunosuppressive Agents