Clinically demonstrable anti-autoimmunity mediated by allogeneic immune cells favorably affects outcome after stem cell transplantation in human autoimmune diseases

Bone Marrow Transplant. 2002 Dec;30(11):753-9. doi: 10.1038/sj.bmt.1703686.

Abstract

To determine the role of allogeneic, autologous and syngeneic hemopoietic stem cell transplantation (SCTx) as a treatment for severe autoimmune disease (AID) we performed a literature search employing Medline, Cancer Lit and abstract books for reports on transplants for blood disorders and a concomitant AID. All reviews, case reports and abstracts available between June 1977 and September 2001 were used and attempts made to update them by e-mail by the corresponding authors. Disease-free survival (DFS) after allogeneic SCTx for 23 patients with severe aplastic anemia was 78% at 16 years and survival in unmaintained remission of concomitant AID was 64% at 13 years. DFS after allogeneic SCTx for 24 patients with hematologic malignancies was 87% at 15 years and survival in unmaintained remission for concomitant AID was 70% at 11 years. DFS after autologous SCTx for 24 patients with hematologic malignancies was 48% at 6 years and survival in unmaintained remission for concomitant AID was 29% at 3 years. Among 30 patients given allogeneic SCTx 19 developed graft-versus-host disease (GVHD) and 11 did not. Upon clinically justified discontinuation of all immunosuppressive therapy, 3/11 patients without GVHD relapsed with their concomitant AID (freedom of AID-relapse 69% at 9 years), whereas none of 19 patients with GVHD did so (log rank: P = 0.0135). Freedom of AID-relapse was superior after allo SCTx compared to autologous SCTx (89% at 18 years vs 38% at 5 years; log rank: P = 0.0002). Our data suggest that a graft-versus-autoimmunity effect after allogeneic hemopoietic SCTx mediates elimination of autoimmunity.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Anemia, Aplastic / complications
  • Anemia, Aplastic / mortality
  • Autoimmune Diseases / complications
  • Autoimmune Diseases / mortality
  • Autoimmune Diseases / therapy*
  • Autoimmunity / immunology
  • Child
  • Data Collection
  • Disease-Free Survival
  • Female
  • Hematologic Neoplasms / complications
  • Hematologic Neoplasms / mortality
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Immune System / cytology
  • Immune System / immunology*
  • Male
  • Middle Aged
  • Prognosis
  • Retrospective Studies
  • Transplantation Conditioning / methods
  • Transplantation, Homologous / immunology
  • Treatment Outcome