Inhibition of hepatitis C virus RNA replication by 2'-modified nucleoside analogs

J Biol Chem. 2003 Apr 4;278(14):11979-84. doi: 10.1074/jbc.M210914200. Epub 2003 Jan 27.

Abstract

The RNA-dependent RNA polymerase (NS5B) of hepatitis C virus (HCV) is essential for the replication of viral RNA and thus constitutes a valid target for the chemotherapeutic intervention of HCV infection. In this report, we describe the identification of 2'-substituted nucleosides as inhibitors of HCV replication. The 5'-triphosphates of 2'-C-methyladenosine and 2'-O-methylcytidine are found to inhibit NS5B-catalyzed RNA synthesis in vitro, in a manner that is competitive with substrate nucleoside triphosphate. NS5B is able to incorporate either nucleotide analog into RNA as determined with gel-based incorporation assays but is impaired in its ability to extend the incorporated analog by addition of the next nucleotide. In a subgenomic replicon cell line, 2-C-methyladenosine and 2'-O-methylcytidine inhibit HCV RNA replication. The 5'-triphosphates of both nucleosides are detected intracellularly following addition of the nucleosides to the media. However, significantly higher concentrations of 2'-C-methyladenosine triphosphate than 2'-O-methylcytidine triphosphate are detected, consistent with the greater potency of 2'-C-methyladenosine in the replicon assay, despite similar inhibition of NS5B by the triphosphates in the in vitro enzyme assays. Thus, the 2'-modifications of natural substrate nucleosides transform these molecules into potent inhibitors of HCV replication.

MeSH terms

  • Adenosine / analogs & derivatives
  • Adenosine / chemistry*
  • Adenosine / pharmacology
  • Adenosine Triphosphate / analogs & derivatives
  • Adenosine Triphosphate / chemistry
  • Cells, Cultured
  • Cytidine / analogs & derivatives*
  • Cytidine / pharmacology*
  • Cytidine Triphosphate / analogs & derivatives
  • Cytidine Triphosphate / chemistry
  • DNA Polymerase I / antagonists & inhibitors
  • DNA Polymerase beta / antagonists & inhibitors
  • DNA Polymerase gamma
  • DNA-Directed DNA Polymerase
  • Gels
  • Hepacivirus / genetics*
  • Hepacivirus / growth & development
  • Hepatitis C / virology*
  • Humans
  • Nucleic Acid Synthesis Inhibitors
  • RNA, Viral / genetics*
  • Viral Nonstructural Proteins / antagonists & inhibitors
  • Viral Nonstructural Proteins / metabolism
  • Virus Replication / drug effects

Substances

  • Gels
  • Nucleic Acid Synthesis Inhibitors
  • RNA, Viral
  • Viral Nonstructural Proteins
  • 2'-O-methylcytidine
  • Cytidine
  • Cytidine Triphosphate
  • Adenosine Triphosphate
  • NS-5 protein, hepatitis C virus
  • DNA Polymerase I
  • DNA Polymerase beta
  • DNA Polymerase gamma
  • DNA-Directed DNA Polymerase
  • Adenosine