Abstract
Objective:
To determine the molecular basis of late onset ornithine transcarbamylase (OTC) deficiency in a Chinese family of Han nationality and the exon sequences of OTC gene of this patient.
Methods:
Polymerase chain reaction-single strand conformation polymorphism and direct sequencing were used to identify the mutation type.
Results:
A missense mutation E122G in the conserved residue of exon 4 was identified which is unreported before.
Conclusion:
The E122G mutation in human OTC gene may cause late onset OTC deficiency.
Publication types
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Case Reports
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English Abstract
MeSH terms
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Age of Onset
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Base Sequence
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Child, Preschool
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DNA / chemistry
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DNA / genetics
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DNA Mutational Analysis
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Family Health
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Fatal Outcome
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Female
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Humans
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Male
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Models, Molecular
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Mutation, Missense
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Ornithine Carbamoyltransferase / chemistry
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Ornithine Carbamoyltransferase / genetics*
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Ornithine Carbamoyltransferase Deficiency Disease / enzymology
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Ornithine Carbamoyltransferase Deficiency Disease / genetics*
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Ornithine Carbamoyltransferase Deficiency Disease / pathology
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Pedigree
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Polymorphism, Single-Stranded Conformational
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Protein Structure, Secondary
Substances
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DNA
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Ornithine Carbamoyltransferase