A score test for establishing non-inferiority with respect to short-term survival in two-sample comparisons with identical proportions of long-term survivors

Stat Med. 2003 Mar 30;22(6):931-40. doi: 10.1002/sim.1453.

Abstract

In recent years randomized trials designed to establish non-inferiority of a new treatment as compared to a standard one have been more widely used. Two-sample statistics have been proposed for this equivalence testing problem. However, they are not suited to situations where a long-term survivor fraction is expected. In this paper we propose a score test designed for establishing non-inferiority for the new treatment as compared to the standard one while assuming identical long-term survivor rates. Simulations results show that the proposed statistic has satisfactory size and power as long as certain restricting conditions are verified. A breast cancer trial is analysed as an example.

Publication types

  • Comparative Study

MeSH terms

  • Breast Neoplasms / radiotherapy
  • Breast Neoplasms / surgery
  • Computer Simulation
  • Female
  • Humans
  • Lymph Nodes / surgery
  • Models, Biological*
  • Models, Statistical*
  • Randomized Controlled Trials as Topic / methods
  • Survival Analysis
  • Therapeutic Equivalency*