Sanglifehrin-cyclophilin interaction: degradation work, synthetic macrocyclic analogues, X-ray crystal structure, and binding data

J Am Chem Soc. 2003 Apr 2;125(13):3849-59. doi: 10.1021/ja021327y.

Abstract

Sanglifehrin A (SFA) is a novel immunosuppressive natural product isolated from Streptomyces sp. A92-308110. SFA has a very strong affinity for cyclophilin A (IC(50) = 6.9 +/- 0.9 nM) but is structurally different from cyclosporin A (CsA) and exerts its immunosuppressive activity via a novel mechanism. SFA has a complex molecular structure consisting of a 22-membered macrocycle, bearing in position 23 a nine-carbon tether terminated by a highly substituted spirobicyclic moiety. Selective oxidative cleavage of the C(26)=C(27) exocyclic double bond affords the spirolactam containing fragment 1 and macrolide 2. The affinity of 2 for cyclophilin (IC(50) = 29 +/- 2.1 nM) is essentially identical to SFA, which indicates that the interaction between SFA and cyclophilin A is mediated exclusively by the macrocyclic portion of the molecule. This observation was confirmed by the X-ray crystal structure resolved at 2.1 A of cyclophilin A complexed to macrolide 16, a close analogue of 2. The X-ray crystal structure showed that macrolide 16 binds to the same deep hydrophobic pocket of cyclophilin A as CsA. Additional valuable details of the structure-activity relationship were obtained by two different chemical approaches: (1) degradation work on macrolide 2 or (2) synthesis of a library of macrolide analogues using the ring-closing metathesis reaction as the key step. Altogether, it appears that the complex macrocyclic fragment of SFA is a highly optimized combination of multiple functionalities including an (E,E)-diene, a short polypropionate fragment, and an unusual tripeptide unit, which together provide an extremely strong affinity for cyclophilin A.

MeSH terms

  • Binding, Competitive
  • Crystallography, X-Ray
  • Cyclophilin A / chemistry*
  • Cyclophilin A / metabolism
  • Immunosuppressive Agents / chemical synthesis
  • Immunosuppressive Agents / chemistry*
  • Immunosuppressive Agents / metabolism
  • Immunosuppressive Agents / pharmacology
  • Kinetics
  • Lactones / chemical synthesis
  • Lactones / chemistry*
  • Lactones / metabolism
  • Lactones / pharmacology
  • Models, Molecular
  • Molecular Structure
  • Signal Transduction / drug effects
  • Spiro Compounds / chemical synthesis
  • Spiro Compounds / chemistry*
  • Spiro Compounds / metabolism
  • Spiro Compounds / pharmacology
  • Structure-Activity Relationship

Substances

  • Immunosuppressive Agents
  • Lactones
  • Spiro Compounds
  • sanglifehrin A
  • Cyclophilin A