Graft-versus-host disease, donor chimerism, and organ toxicity in stem cell transplantation after conditioning with fludarabine and melphalan

Biol Blood Marrow Transplant. 2003 Jul;9(7):435-42. doi: 10.1016/s1083-8791(03)00128-9.

Abstract

Hematopoietic stem cell transplantation may be used to induce a graft-versus-tumor effect against a range of malignancies. Pretransplantation conditioning regimens vary considerably in their degree of myelosuppression and immunosuppression, which may result in marked differences in the rate of T-cell engraftment and, as a consequence, the onset and severity of graft-versus-host disease (GVHD). We have examined the development of T-cell chimerism and the onset of GVHD following fludarabine and melphalan conditioning in 39 patients undergoing stem cell allografts from matched-sibling donors. Cyclosporin and short-course methotrexate were used as GVHD prophylaxis. Fatal regimen-related toxicity occurred in 4 patients. Rapid T-cell engraftment was found in all but 1 of the patients assessed, with more than 90% donor T-cell chimerism at 1 month posttransplantation. Of the evaluable patients, 43% developed grade 2-4 acute GVHD and 87% developed chronic GVHD (70% extensive). Overall, the combination of fludarabine and melphalan is intensely immunosuppressive, leads to rapid T-cell engraftment and results in substantial toxicity and GVHD, particularly in heavily pretreated patients.

Publication types

  • Clinical Trial

MeSH terms

  • Adult
  • Aged
  • Disease-Free Survival
  • Female
  • Graft vs Host Disease / etiology*
  • Graft vs Tumor Effect / drug effects
  • Hematopoietic Stem Cell Transplantation / adverse effects*
  • Hematopoietic Stem Cell Transplantation / mortality
  • Humans
  • Immunosuppressive Agents / adverse effects
  • Immunosuppressive Agents / therapeutic use*
  • Male
  • Melphalan / adverse effects
  • Melphalan / therapeutic use*
  • Middle Aged
  • Time Factors
  • Transplantation Chimera*
  • Transplantation Conditioning / methods*
  • Transplantation, Homologous
  • Vidarabine / adverse effects
  • Vidarabine / analogs & derivatives*
  • Vidarabine / therapeutic use*

Substances

  • Immunosuppressive Agents
  • Vidarabine
  • fludarabine
  • Melphalan