Detection and quantitation of acylcarnitines in plasma and blood spots from patients with inborn errors of fatty acid oxidation

Prog Clin Biol Res. 1992:375:355-62.

Abstract

Acylcarnitine profiling in plasma and dried blood spots by radioisotopic exchange/HPLC demonstrates that MCAD deficiency can be reliably detected in the asymptomatic state without L-carnitine therapy. The OC/AcC ratio differentiates MCAD deficiency from normal controls. A longer chain acylcarnitine (r.t. 43 min.) was detected in all 3 patients with a defect in long chain fatty acid oxidation. Detection of C4- and C5-acylcarnitine isomers in plasma helped characterize a metabolic defect affecting branched chain acyl-CoA oxidation in 3 patients. Quantitative data in 2 patients with MCAD deficiency showed that plasma concentrations of OC and AcC are dependent on both the availability of free carnitine and the severity of metabolic decompensation.

MeSH terms

  • Acyl-CoA Dehydrogenase
  • Acyl-CoA Dehydrogenase, Long-Chain / deficiency
  • Blood Stains
  • Carnitine / blood*
  • Fatty Acids / metabolism*
  • Humans
  • Metabolism, Inborn Errors / blood*
  • Oxidation-Reduction
  • Stereoisomerism

Substances

  • Fatty Acids
  • Acyl-CoA Dehydrogenase
  • Acyl-CoA Dehydrogenase, Long-Chain
  • Carnitine