Homozygous familial hypercholesterolemia: specific indication for domino liver transplantation

Transplantation. 2003 Nov 15;76(9):1345-50. doi: 10.1097/01.TP.0000093996.96158.44.

Abstract

Background: Domino liver transplantation is one possibility to overcome the discrepancy between the small number of liver donors and the long waiting lists. Homozygous familial hypercholesterolemia (FHC) is a genetic disorder of lipoprotein metabolism defined by the absence or small number of functional low-density lipoprotein receptors (LDL-Rs) and the ensuing high levels of serum cholesterol. We report a case of a patient with FHC whose liver was used for domino transplantation in a patient with cirrhosis and hepatocellular carcinoma.

Methods: The patient diagnosed with FHC received the large part of a split liver. The liver of the patient with FHC was then transplanted into the patient with cirrhosis and hepatocellular carcinoma. Quantification of extrahepatic LDL-R was performed by flow cytometry on monocytes, and the gene expression of LDL-R was assayed by reverse transcriptase-polymerase chain reaction on monocyte-derived macrophages and cultured fibroblasts isolated from the patients.

Results: One year after surgery, the donor's serum cholesterol (without treatment) was normal, and the recipient's serum cholesterol (with simvastatin treatment) was slightly increased. Quantification of peripheral LDL-R on monocytes isolated from the patients revealed values of 6.7% in the patient with FHC and 71% in the patient with cirrhosis and hepatocellular carcinoma. The reverse transcriptase-polymerase chain reaction assay revealed the presence of gene expression for LDL-R.

Conclusions: Domino transplantation can be efficiently used in a patient with marginal indications for transplantation using a liver from a patient with FHC. The slightly elevated serum cholesterol level in the recipient may be explained by the normal function of extrahepatic LDL-R.

Publication types

  • Case Reports

MeSH terms

  • Female
  • Hepatectomy* / methods
  • Hepatitis B / surgery*
  • Homozygote*
  • Humans
  • Hyperlipoproteinemia Type II / genetics*
  • Hyperlipoproteinemia Type II / surgery*
  • Liver Neoplasms / surgery*
  • Liver Transplantation / methods*
  • Living Donors
  • Male
  • Middle Aged
  • Pedigree
  • Receptors, LDL / blood
  • Receptors, LDL / genetics
  • Reverse Transcriptase Polymerase Chain Reaction
  • Tissue and Organ Harvesting / methods

Substances

  • Receptors, LDL