A natural prothrombin mutant reveals an unexpected influence of A-chain structure on the activity of human alpha-thrombin

J Biol Chem. 2004 Mar 26;279(13):13035-43. doi: 10.1074/jbc.M312430200. Epub 2004 Jan 13.

Abstract

We have recently identified in two unrelated patients with bleeding tendency a homozygous mutation causing a deletion of one of the two contiguous Lys(9)/Lys(10) residues in the A-chain of alpha-thrombin (DeltaK9). We used in vitro expression analysis to clarify the role of the deletion of Lys(9) or Lys(10) in the thrombin function. The k(cat)/K(m) value of the hydrolysis by DeltaK9 of the synthetic substrate Phe-Pip-Arg-p-nitroanilide (where Pip represents l-pipecolyl) and fibrinopeptide A was 18- and 60-fold lower, respectively, compared with wild type (WT). Interaction with antithrombin was also reduced in the mutant, the association rate being about 20-fold lower than in the WT thrombin. The sensitivity to sodium ion of DeltaK9 was found significantly attenuated compared with the WT form. DeltaK9 has a very weak platelet-activating capacity, attributed to a severely defective PAR1 interaction, whereas the binding to the platelet glycoprotein Ibalpha was unaffected. Likewise, the interaction with protein C was severely impaired, whereas interaction with thrombomodulin had a normal K(d) value. At variance with these findings, both low affinity (basic pancreatic trypsin inhibitor) and high affinity (N-alpha-[2-naphthylsulfonyl-glycyl]-4-amidinophenylalanine-piperidide) thrombin inhibitors displayed a better binding to DeltaK9 than to the WT form, indicating a better accommodation of these inhibitors into the catalytic pocket of DeltaK9. A molecular dynamics simulation of the DeltaK9 thrombin in full explicit water solvent provided support to the role of the A-chain in affecting conformation and catalytic properties of the B-chain, especially in some insertion loops of the enzyme, such as the 60-loop, as well as in the geometry of the catalytic triad residues.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Arginine / analogs & derivatives*
  • Arginine / chemistry
  • Blood Platelets / metabolism
  • COS Cells
  • Catalytic Domain
  • Cell Membrane / metabolism
  • Chromatography, High Pressure Liquid
  • DNA / chemistry
  • Fibrinogen / chemistry
  • Fibrinopeptide A / chemistry
  • Gene Deletion
  • Humans
  • Hydrolysis
  • Hypoprothrombinemias / metabolism*
  • Ions
  • Kinetics
  • Lysine / chemistry
  • Models, Molecular
  • Mutagenesis, Site-Directed
  • Mutation
  • Protein Binding
  • Protein C / chemistry
  • Protein Conformation
  • Protein Structure, Secondary
  • Prothrombin / genetics*
  • Sodium / chemistry
  • Sodium Chloride / pharmacology
  • Thrombin / chemistry*
  • Thrombin / metabolism
  • Time Factors
  • Transfection

Substances

  • Ions
  • Protein C
  • Fibrinopeptide A
  • Sodium Chloride
  • arginine-4-nitroanilide
  • Prothrombin
  • Fibrinogen
  • DNA
  • Arginine
  • Sodium
  • Thrombin
  • Lysine