Hyperparathyroidism-jaw tumor syndrome in Roma families from Portugal is due to a founder mutation of the HRPT2 gene

J Clin Endocrinol Metab. 2004 Apr;89(4):1747-52. doi: 10.1210/jc.2003-031016.

Abstract

The hyperparathyroidism-jaw tumor (HPT-JT) syndrome is an autosomal dominant disorder characterized by the occurrence of parathyroid tumors and ossifying jaw fibromas. The gene causing HPT-JT, HRPT2, is located on chromosome 1q31.2 and consists of 17 exons that encode a 531-amino acid protein, designated parafibromin. We recently identified six Roma families in Portugal with 56 members (11 affected and 45 asymptomatic), who had the HPT-JT syndrome. We postulated that they may have a common ancestor and that the HPT-JT syndrome may be due to a mutation of the HRPT2 gene. Haplotype analysis using 14 chromosome 1q24-q32 polymorphic markers showed that the 11 affected individuals shared a common haplotype defined by seven markers that spanned an approximately 12.5-cM region, flanked centromerically by D1S202 and telomerically by D1S306. DNA sequence analysis identified a 2-bp (TG or GT) frameshift deletion in exon 8, which predicts a truncated parafibromin protein, in all 11 affected individuals. This mutation was also found in 19 unaffected individuals (age range, 12-74 yr) who shared the affected haplotype, suggesting a low age-related penetrance for HPT-JT in these families. Thus, the HPT-JT syndrome in six Roma families from Portugal is due to a novel founder mutation in the HRPT2 gene.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Aging
  • DNA / genetics
  • Female
  • Founder Effect*
  • Haplotypes
  • Humans
  • Hyperparathyroidism / genetics*
  • Jaw Neoplasms / genetics*
  • Male
  • Middle Aged
  • Mutation*
  • Pedigree
  • Penetrance
  • Portugal
  • Proteins / genetics*
  • Sex Characteristics
  • Syndrome
  • Tumor Suppressor Proteins

Substances

  • CDC73 protein, human
  • Proteins
  • Tumor Suppressor Proteins
  • DNA