Novel TSHbeta subunit gene mutation causing congenital central hypothyroidism in a newborn male

J Pediatr Endocrinol Metab. 2004 Mar;17(3):355-9. doi: 10.1515/jpem.2004.17.3.355.

Abstract

Newborn screening programs that use only high TSH levels as a marker for hypothyroidism may overlook neonates with congenital hypothyroidism (CH) due to TSH deficiency. We sought the cause of TSH deficiency in a neonate with low levels of thyroxine and TSH. The coding region of the TSHbeta gene was amplified and its sequence examined for mutations. Two mutations in exon 3 were identified: 1) a nucleotide deletion of T410 in codon 105 resulting in a frameshift in one allele, and 2) a previously unreported nucleotide deletion of T266 in codon 57, causing a frameshift and a premature stop at codon 62 in the other allele. We describe a compound heterozygous patient with TSHbeta mutations at codons 57 and 105 that interfered with a critical disulfide bond in the TSH molecule and caused CH. State screening programs that measure both T4 and TSH levels have the potential to detect newborns with congenital central hypothyroidism.

Publication types

  • Case Reports

MeSH terms

  • Congenital Hypothyroidism*
  • Fertilization in Vitro
  • Heterozygote
  • Hormone Replacement Therapy
  • Humans
  • Hypothyroidism / drug therapy
  • Hypothyroidism / genetics*
  • Infant, Newborn
  • Infusions, Intravenous
  • Male
  • Mutation*
  • Sequence Analysis, DNA
  • Thyrotropin, beta Subunit / blood
  • Thyrotropin, beta Subunit / deficiency*
  • Thyrotropin, beta Subunit / genetics*
  • Thyrotropin-Releasing Hormone / pharmacology
  • Thyrotropin-Releasing Hormone / therapeutic use
  • Thyroxine / blood
  • Thyroxine / therapeutic use
  • Time Factors
  • Treatment Outcome

Substances

  • Thyrotropin, beta Subunit
  • Thyrotropin-Releasing Hormone
  • Thyroxine