Barth syndrome without 3-methylglutaconic aciduria

Acta Paediatr. 2004 Mar;93(3):419-21. doi: 10.1080/08035250410022837.

Abstract

Barth syndrome involves cardiomyopathy, skeletal myopathy, neutropenia and 3-methylglutaconic (3-mgc) aciduria. 3-mgc aciduria has been observed in almost all reported cases and has served as a diagnostic criterion.

Conclusion: A case of confirmed BTHS, but without 3-mgc aciduria, emphasizes the importance of extensive investigations in cases with suspected hereditary cardiomyopathy.

Publication types

  • Case Reports

MeSH terms

  • Arginine / genetics
  • Cardiomyopathies / diagnosis
  • Cardiomyopathies / genetics*
  • Chromosomes, Human, X
  • Fatal Outcome
  • Glutarates
  • Glycine / genetics
  • Humans
  • Infant, Newborn
  • Male
  • Muscular Diseases / diagnosis
  • Muscular Diseases / genetics*
  • Mutation
  • Mutation, Missense*
  • Pedigree
  • Syndrome

Substances

  • Glutarates
  • 3-methylglutaconic acid
  • Arginine
  • Glycine