Central core disease mutations R4892W, I4897T and G4898E in the ryanodine receptor isoform 1 reduce the Ca2+ sensitivity and amplitude of Ca2+-dependent Ca2+ release

Biochem J. 2004 Sep 1;382(Pt 2):557-64. doi: 10.1042/BJ20040580.

Abstract

Three CCD (central core disease) mutants, R4892W (Arg4892-->), I4897T and G4898E, in the pore region of the skeletal-muscle Ca2+-release channel RyR1 (ryanodine receptor 1) were characterized using a newly developed assay that monitored Ca2+ release in the presence of Ca2+ uptake in microsomes isolated from HEK-293 cells (human embryonic kidney 293 cells), co-expressing each of the three mutants together with SERCA1a (sarcoplasmic/endoplasmic-reticulum Ca2+-ATPase 1a). Both Ca2+ sensitivity and peak amplitude of Ca2+ release were either absent from or sharply decreased in homotetrameric mutants. Co-expression of wild-type RyR1 with mutant RyR1 (heterotetrameric mutants) restored Ca2+ sensitivity partially, in the ratio 1:2, or fully, in the ratio 1:1. Peak amplitude was restored only partially in the ratio 1:2 or 1:1. Reduced amplitude was not correlated with maximum Ca2+ loading or the amount of expressed RyR1 protein. High-affinity [3H]ryanodine binding and caffeine-induced Ca2+ release were also absent from the three homotetrameric mutants. These results indicate that decreased Ca2+ sensitivity is one of the serious defects in these three excitation-contraction uncoupling CCD mutations. In CCD skeletal muscles, where a mixture of wild-type and mutant RyR1 is expressed, these defects are expected to decrease Ca2+-induced Ca2+ release, as well as orthograde Ca2+ release, in response to transverse tubular membrane depolarization.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Triphosphate / metabolism
  • Arginine / genetics
  • Calcium / chemistry
  • Calcium / metabolism
  • Calcium Isotopes / metabolism
  • Calcium-Transporting ATPases / biosynthesis
  • Cell Line
  • Glutamic Acid / genetics
  • Glycine / genetics
  • Humans
  • Isoleucine / metabolism
  • Kidney / chemistry
  • Kidney / cytology
  • Kidney / embryology
  • Kidney / metabolism
  • Microsomes / chemistry
  • Microsomes / metabolism
  • Mutagenesis, Site-Directed
  • Mutation, Missense / genetics*
  • Myopathy, Central Core / genetics*
  • Oxalates / metabolism
  • Photometry / methods
  • Protein Isoforms / genetics
  • Ryanodine Receptor Calcium Release Channel / biosynthesis
  • Ryanodine Receptor Calcium Release Channel / genetics*
  • Ryanodine Receptor Calcium Release Channel / metabolism
  • Sarcoplasmic Reticulum Calcium-Transporting ATPases
  • Threonine / genetics
  • Tryptophan / genetics

Substances

  • Calcium Isotopes
  • Oxalates
  • Protein Isoforms
  • Ryanodine Receptor Calcium Release Channel
  • Isoleucine
  • Threonine
  • Glutamic Acid
  • Tryptophan
  • Adenosine Triphosphate
  • Arginine
  • Sarcoplasmic Reticulum Calcium-Transporting ATPases
  • Calcium-Transporting ATPases
  • Calcium
  • Glycine