The size of sinusoidal fenestrae is a critical determinant of hepatocyte transduction after adenoviral gene transfer

Gene Ther. 2004 Oct;11(20):1523-31. doi: 10.1038/sj.gt.3302326.

Abstract

The hepatotropism and intrahepatic distribution of adenoviral vectors may be species dependent. Hepatocyte transduction was evaluated in three rabbit strains after transfer with E1E3E4-deleted adenoviral vectors containing a hepatocyte specific alpha1-antitrypsin promoter-driven expression cassette (AdAT4). Intravenous administration of 4 x 10(12) particles/kg of AdAT4 induced human apo A-I levels above 40 mg/dl in Dutch Belt, but below 1 mg/dl in New Zealand White and Fauve de Bourgogne rabbits. Diameters of sinusoidal fenestrae were significantly (P=0.0014) larger in Dutch Belt (124+/-3.4 nm) than in New Zealand White (108+/-1.3 nm) and Fauve de Bourgogne (105+/-2.6 nm) rabbits, suggesting that a smaller size constitutes a barrier for hepatocyte transduction. Indeed, intraportal transfer preceded by intraportal injection of sodium decanoate, which increases the diameter of sinusoidal fenestrae to 123+/-3.4 nm (P<0.01) in New Zealand White rabbits, increased human apo A-I levels 32- and 120-fold in New Zealand White and Fauve de Bourgogne rabbits, respectively, but did not affect expression in Dutch Belt rabbits. In conclusion, size of sinusoidal fenestrae appears to be a critical determinant of hepatocyte transduction after adenoviral transfer.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae / genetics*
  • Animals
  • Apolipoprotein A-I / genetics*
  • Apolipoprotein A-I / metabolism
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage*
  • Hepatocytes / metabolism
  • Humans
  • Liver / ultrastructure*
  • Male
  • Microscopy, Electron, Transmission
  • Rabbits
  • Species Specificity
  • Transduction, Genetic / methods*
  • Transgenes

Substances

  • Apolipoprotein A-I