A novel mutation of WT1 exon 9 in a patient with Denys-Drash syndrome and pyloric stenosis

Pediatr Nephrol. 2004 Oct;19(10):1160-3. doi: 10.1007/s00467-004-1564-3. Epub 2004 Jul 28.

Abstract

We report a novel mutation in WT1 exon 9 (1214 A>G) resulting in an amino acid change from H to R at codon 405 in a 46 XY female patient who had congenital hypertrophic pyloric stenosis, pseudohermaphroditism masculinus, renal failure, and Wilms tumor, and died at the age of 22 months. The patient demonstrated the difficulty in diagnosing a patient with intersex before conclusive genetic characterization.

Publication types

  • Case Reports

MeSH terms

  • Denys-Drash Syndrome / complications
  • Denys-Drash Syndrome / genetics*
  • Disorders of Sex Development / diagnosis
  • Disorders of Sex Development / genetics
  • Fatal Outcome
  • Female
  • Genes, Wilms Tumor*
  • Humans
  • Infant
  • Mutation
  • Pyloric Stenosis, Hypertrophic / complications
  • Pyloric Stenosis, Hypertrophic / congenital
  • Renal Insufficiency / etiology