Small molecule modulators of endogenous and co-chaperone-stimulated Hsp70 ATPase activity

J Biol Chem. 2004 Dec 3;279(49):51131-40. doi: 10.1074/jbc.M404857200. Epub 2004 Sep 23.

Abstract

The molecular chaperone and cytoprotective activities of the Hsp70 and Hsp40 chaperones represent therapeutic targets for human diseases such as cancer and those that arise from defects in protein folding; however, very few Hsp70 and no Hsp40 modulators have been described. Using an assay for ATP hydrolysis, we identified and screened small molecules with structural similarity to 15-deoxyspergualin and NSC 630668-R/1 for their effects on endogenous and Hsp40-stimulated Hsp70 ATPase activity. Several of these compounds modulated Hsp70 ATPase activity, consistent with the action of NSC 630668-R/1 observed previously (Fewell, S. W., Day, B. W., and Brodsky, J. L. (2001) J. Biol. Chem. 276, 910-914). In contrast, three compounds inhibited the ability of Hsp40 to stimulate Hsp70 ATPase activity but did not affect the endogenous activity of Hsp70. Two of these agents also compromised the Hsp70/Hsp40-mediated post-translational translocation of a secreted pre-protein in vitro. Together, these data indicate the potential for continued screening of small molecule Hsp70 effectors and that specific modulators of Hsp70-Hsp40 interaction can be obtained, potentially for future therapeutic use.

Publication types

  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adenosine Triphosphatases / chemistry
  • Adenosine Triphosphate / chemistry
  • Antibiotics, Antineoplastic / pharmacology
  • Biological Transport
  • Dose-Response Relationship, Drug
  • Guanidines / pharmacology
  • HSP40 Heat-Shock Proteins
  • HSP70 Heat-Shock Proteins / chemistry
  • HSP70 Heat-Shock Proteins / physiology*
  • Heat-Shock Proteins / chemistry*
  • Humans
  • Hydrolysis
  • Models, Chemical
  • Models, Molecular
  • Molecular Chaperones / chemistry*
  • Protein Binding
  • Protein Conformation
  • Protein Processing, Post-Translational
  • Protein Transport
  • Software
  • Structure-Activity Relationship
  • Thermodynamics
  • Time Factors

Substances

  • Antibiotics, Antineoplastic
  • DNAJB1 protein, human
  • Guanidines
  • HSP40 Heat-Shock Proteins
  • HSP70 Heat-Shock Proteins
  • Heat-Shock Proteins
  • Molecular Chaperones
  • Adenosine Triphosphate
  • Adenosine Triphosphatases
  • gusperimus