Restoration of ureagenesis in N-acetylglutamate synthase deficiency by N-carbamylglutamate

J Pediatr. 2004 Oct;145(4):552-4. doi: 10.1016/j.jpeds.2004.06.047.

Abstract

In a patient with N-acetylglutamate synthase (NAGS) deficiency, incorporation of an isotopic label from ammonium chloride into urea was markedly reduced before treatment with N-carbamyl-L-glutamate (NCLG) and completely normalized following treatment. Blood ammonia rose following ammonium tracer ingestion before treatment but remained low following treatment. Serum urea concentration doubled following the treatment.

Publication types

  • Case Reports
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Acetyltransferases / deficiency*
  • Acetyltransferases / genetics
  • Adolescent
  • Adult
  • Amino-Acid N-Acetyltransferase
  • Ammonia / blood
  • Ammonium Chloride / pharmacokinetics
  • Blood Urea Nitrogen
  • Female
  • Glutamates / therapeutic use*
  • Glutamine / blood
  • Humans
  • Nitrogen Isotopes / pharmacokinetics
  • Urea / metabolism*

Substances

  • Glutamates
  • Nitrogen Isotopes
  • Ammonium Chloride
  • Glutamine
  • N-carbamylglutamate
  • Ammonia
  • Urea
  • Acetyltransferases
  • Amino-Acid N-Acetyltransferase
  • NAGS protein, human