Targeting gene expression selectively in cancer cells by using the progression-elevated gene-3 promoter

Proc Natl Acad Sci U S A. 2005 Jan 25;102(4):1059-64. doi: 10.1073/pnas.0409141102. Epub 2005 Jan 12.

Abstract

One impediment to effective cancer-specific gene therapy is the rarity of regulatory sequences targeting gene expression selectively in tumor cells. Although many tissue-specific promoters are recognized, few cancer-selective gene promoters are available. Progression-elevated gene-3 (PEG-3) is a rodent gene identified by subtraction hybridization that displays elevated expression as a function of transformation by diversely acting oncogenes, DNA damage, and cancer cell progression. The promoter of PEG-3, PEG-Prom, displays robust expression in a broad spectrum of human cancer cell lines with marginal expression in normal cellular counterparts. Whereas GFP expression, when under the control of a CMV promoter, is detected in both normal and cancer cells, when GFP is expressed under the control of the PEG-Prom, cancer-selective expression is evident. Mutational analysis identifies the AP-1 and PEA-3 transcription factors as primary mediators of selective, cancer-specific expression of the PEG-Prom. Synthesis of apoptosis-inducing genes, under the control of the CMV promoter, inhibits the growth of both normal and cancer cells, whereas PEG-Prom-mediated expression of these genes kills only cancer cells and spares normal cells. The efficacy of the PEG-Prom as part of a cancer gene therapeutic regimen is further documented by in vivo experiments in which PEG-Prom-controlled expression of an apoptosis-inducing gene completely inhibited prostate cancer xenograft growth in nude mice. These compelling observations indicate that the PEG-Prom, with its cancer-specific expression, provides a means of selectively delivering genes to cancer cells, thereby providing a crucial component in developing effective cancer gene therapies.

MeSH terms

  • Animals
  • Antigens, Differentiation / genetics*
  • Cell Cycle Proteins
  • Genes, Tumor Suppressor
  • Genetic Therapy*
  • Humans
  • Interleukins / genetics
  • Male
  • Mice
  • Neoplasm Proteins / genetics*
  • Neoplasms / therapy*
  • Promoter Regions, Genetic
  • Protein Phosphatase 1
  • Proteins / genetics
  • Proto-Oncogene Proteins
  • Transcription Factor AP-1 / physiology
  • Transcription Factors / physiology

Substances

  • Antigens, Differentiation
  • Cell Cycle Proteins
  • Interleukins
  • Neoplasm Proteins
  • Ppp1r15a protein, rat
  • Proteins
  • Proto-Oncogene Proteins
  • Transcription Factor AP-1
  • Transcription Factors
  • interleukin-24
  • transcription factor PEA3
  • PPP1R15A protein, human
  • Ppp1r15a protein, mouse
  • Protein Phosphatase 1