AAV2/5-mediated NGF gene delivery protects septal cholinergic neurons following axotomy

Brain Res. 2005 Nov 9;1061(2):107-13. doi: 10.1016/j.brainres.2005.08.056. Epub 2005 Oct 14.

Abstract

Nerve growth factor (NGF) therapy has been proposed to treat cognitive impairments in aged patients including those with Alzheimer's disease. Various viral vectors, including adeno-associated virus serotype 2 (AAV2), have been investigated for their ability to deliver NGF in brain. In this study, hybrid vectors (AAV2/5) consisting of the genome of recombinant AAV2 and the capsid of AAV serotype 5 were evaluated for their ability to deliver NGF and green fluorescent protein (GFP) genes into brain. Compared to AAV2, AAV2/5 consistently led to more septal neurons being transduced with GFP over a wider range of distribution. However, both types of vector provided similar levels of long-term (17 weeks) protection of septal cholinergic neurons from axotomy and led to similar levels of NGF accumulation in this region. These results demonstrate that rAAV-mediated NGF gene delivery is neuroprotective for an extended period of time, but that factors other than transduction efficiency appear to determine transgenic NGF expression in septum.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Animals
  • Axotomy*
  • Capsid Proteins / genetics*
  • Choline O-Acetyltransferase / genetics
  • Choline O-Acetyltransferase / metabolism
  • Enzyme-Linked Immunosorbent Assay
  • Fornix, Brain / physiology
  • Genes, Reporter / genetics
  • Genetic Vectors*
  • Green Fluorescent Proteins / genetics
  • Immunohistochemistry
  • Male
  • Nerve Growth Factors / genetics*
  • Parasympathetic Nervous System / physiology*
  • Rats
  • Rats, Sprague-Dawley
  • Septum of Brain / physiology*
  • Stereotaxic Techniques

Substances

  • Capsid Proteins
  • Nerve Growth Factors
  • hexon capsid protein, Adenovirus
  • Green Fluorescent Proteins
  • Choline O-Acetyltransferase