Leucodysplasia, microcephaly, cerebral malformation (LMC): a novel recessive disorder linked to 2p16

Brain. 2006 Jan;129(Pt 1):272-7. doi: 10.1093/brain/awh663. Epub 2005 Nov 4.

Abstract

We report three related and one unrelated child with an apparently novel neurodevelopmental disorder. The clinical course was very similar in all the four patients: congenital microcephaly with severe failure of post-natal brain growth, neonatal onset of intractable seizures associated with lack of developmental progression and death within the first 3 years of life. The appearance on cerebral neuroimaging was almost identical, with simplified gyration associated with a non-thickened cortex, severe hypoplasia of the corpus callosum, a small flattened brain stem, and specific cystic lesions in the white matter around the temporal and occipital horns. To our knowledge these patients represent a previously unreported, autosomal recessive syndrome. Homozygosity mapping in the consanguineous family has identified a candidate region on the chromosome 2p16.

Publication types

  • Case Reports

MeSH terms

  • Abnormalities, Multiple / genetics*
  • Abnormalities, Multiple / pathology
  • Brain / abnormalities*
  • Cerebral Ventricles / abnormalities
  • Cerebral Ventricles / pathology
  • Chromosomes, Human, Pair 2
  • Consanguinity
  • Facies
  • Female
  • Genes, Recessive
  • Genetic Markers
  • Genotype
  • Homozygote
  • Humans
  • Infant, Newborn
  • Magnetic Resonance Imaging
  • Male
  • Microcephaly / genetics*
  • Microcephaly / pathology
  • Pedigree
  • Polymorphism, Single Nucleotide / genetics
  • Seizures / genetics*
  • Seizures / pathology
  • Syndrome

Substances

  • Genetic Markers