Major myofibrillar changes in early onset myopathy due to de novo heterozygous missense mutation in lamin A/C gene

Neuromuscul Disord. 2005 Dec;15(12):847-50. doi: 10.1016/j.nmd.2005.09.007. Epub 2005 Nov 8.

Abstract

Mutations in the lamin A/C gene (LMNA) have been associated with neuromuscular diseases and more complex syndromes, involving bone and adipose tissue. We report on a case of early onset myopathy due to a heterozygous LMNA mutation in exon 9, characterized by the presence of a marked number of cytoplasmic bodies with extensive myofibrillar abnormalities and Z-disk disruption in skeletal muscle. This case suggests there is a need to increase the list of genes to be screened in patients with myofibrillar myopathy.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child
  • DNA Mutational Analysis / methods
  • Desmin / metabolism
  • Electron Transport Complex IV / metabolism
  • Exons
  • Female
  • Humans
  • Immunohistochemistry / methods
  • Lamin Type A / genetics*
  • Muscular Diseases / genetics*
  • Muscular Diseases / metabolism
  • Mutation, Missense / genetics*
  • Myofibrils / metabolism
  • Myofibrils / pathology*
  • Myofibrils / ultrastructure

Substances

  • Desmin
  • LMNA protein, human
  • Lamin Type A
  • Electron Transport Complex IV