Genetic design of an optimized packaging cell line for gene vectors transducing human B cells

Gene Ther. 2006 May;13(10):844-56. doi: 10.1038/sj.gt.3302714.

Abstract

Viral gene vectors often rely on packaging cell lines, which provide the necessary factors in trans for the formation of virus-like particles. Previously, we reported on a first-generation packaging cell line for gene vectors, which are based on the B-lymphotropic Epstein-Barr virus (EBV), a human gamma-herpesvirus. This 293HEK-derived packaging cell line harbors a helper virus genome with a genetic modification that prevents the release of helper virions, but efficiently packages vector plasmids into virus-like particles with transducing capacity for human B cells. Here, we extended this basic approach towards a non-transforming, virus-free packaging cell line, which harbors an EBV helper virus genome with seven genetic alterations. In addition, we constructed a novel gene vector plasmid, which is devoid of a prokaryotic antibiotic resistance gene, and thus more suitable for in vivo applications in human gene therapy. We demonstrate in this paper that EBV-based gene vectors can be efficiently generated with this much-improved packaging cell line to provide helper virus-free gene vector stocks with transducing capacity for established human B-cell lines and primary B cells.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • B-Lymphocytes / virology*
  • Cell Line
  • DNA, Viral / analysis
  • Flow Cytometry
  • Gene Expression
  • Genetic Engineering*
  • Genetic Vectors / genetics*
  • Green Fluorescent Proteins / genetics
  • Helper Viruses
  • Herpesvirus 4, Human
  • Humans
  • Polymerase Chain Reaction
  • Recombination, Genetic
  • Transduction, Genetic / methods*
  • Transfection / methods
  • Virus Assembly*

Substances

  • DNA, Viral
  • Green Fluorescent Proteins