The P174L mutation in human Sco1 severely compromises Cox17-dependent metallation but does not impair copper binding

J Biol Chem. 2006 May 5;281(18):12270-6. doi: 10.1074/jbc.M600496200. Epub 2006 Mar 6.

Abstract

Sco1 is a metallochaperone that is required for copper delivery to the Cu(A) site in the CoxII subunit of cytochrome c oxidase. The only known missense mutation in human Sco1, a P174L substitution in the copper-binding domain, is associated with a fatal neonatal hepatopathy; however, the molecular basis for dysfunction of the protein is unknown. Immortalized fibroblasts from a SCO1 patient show a severe deficiency in cytochrome c oxidase activity that was partially rescued by overexpression of P174L Sco1. The mutant protein retained the ability to bind Cu(I) and Cu(II) normally when expressed in bacteria, but Cox17-mediated copper transfer was severely compromised both in vitro and in a yeast cytoplasmic assay. The corresponding P153L substitution in yeast Sco1 was impaired in suppressing the phenotype of cells harboring the weakly functional C57Y allele of Cox17; however, it was functional in sco1delta yeast when the wild-type COX17 gene was present. Pulse-chase labeling of mitochondrial translation products in SCO1 patient fibroblasts showed no change in the rate of CoxII translation, but there was a specific and rapid turnover of CoxII protein in the chase. These data indicate that the P174L mutation attenuates a transient interaction with Cox17 that is necessary for copper transfer. They further suggest that defective Cox17-mediated copper metallation of Sco1, as well as the subsequent failure of Cu(A) site maturation, is the basis for the inefficient assembly of the cytochrome c oxidase complex in SCO1 patients.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Binding Sites
  • Carrier Proteins / metabolism*
  • Copper / chemistry*
  • Copper / metabolism
  • Copper Transport Proteins
  • Electron Transport Complex IV / metabolism
  • Fibroblasts / metabolism
  • Humans
  • Membrane Proteins / deficiency*
  • Membrane Proteins / genetics
  • Membrane Proteins / physiology*
  • Mitochondria / metabolism
  • Molecular Chaperones
  • Mutation*
  • Mutation, Missense
  • Protein Binding
  • Recombinant Proteins / chemistry

Substances

  • COX17 protein, human
  • Carrier Proteins
  • Copper Transport Proteins
  • Membrane Proteins
  • Molecular Chaperones
  • Recombinant Proteins
  • SCO1 protein, human
  • Copper
  • cytochrome C oxidase subunit II
  • Electron Transport Complex IV