Granulocyte-colony stimulating factor is neuroprotective in a model of Parkinson's disease

J Neurochem. 2006 May;97(3):675-86. doi: 10.1111/j.1471-4159.2006.03727.x. Epub 2006 Mar 29.

Abstract

We have recently shown that the hematopoietic Granulocyte-Colony Stimulating Factor (G-CSF) is neuroprotective in rodent stroke models, and that this action appears to be mediated via a neuronal G-CSF receptor. Here, we report that the G-CSF receptor is expressed in rodent dopaminergic substantia nigra neurons, suggesting that G-CSF might be neuroprotective for dopaminergic neurons and a candidate molecule for the treatment of Parkinson's disease. Thus, we investigated protective effects of G-CSF in 1-methyl-4-phenylpyridinium (MPP+)-challenged PC12 cells and primary neuronal midbrain cultures, as well as in the mouse 1-methyl-4-phenyl-1,2,3,6-tetrahydropyridine (MPTP) model of Parkinson's disease. Substantial protection was found against MPP+-induced dopaminergic cell death in vitro. Moreover, subcutaneous application of G-CSF at a dose of 40 microg/Kg body weight daily over 13 days rescued dopaminergic substantia nigra neurons from MPTP-induced death in aged mice, as shown by quantification of tyrosine hydroxylase-positive substantia nigra cells. Using HPLC, a corresponding reduction in striatal dopamine depletion after MPTP application was observed in G-CSF-treated mice. Thus our data suggest that G-CSF is a novel therapeutic opportunity for the treatment of Parkinson's disease, because it is well-tolerated and already approved for the treatment of neutropenic conditions in humans.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • 1-Methyl-4-phenyl-1,2,3,6-tetrahydropyridine
  • 3,4-Dihydroxyphenylacetic Acid / metabolism
  • Animals
  • Blotting, Northern / methods
  • Brain / cytology
  • Brain / drug effects
  • Brain / metabolism
  • Cell Count / methods
  • Cells, Cultured
  • Chromatography, High Pressure Liquid / methods
  • Disease Models, Animal
  • Dopamine / metabolism
  • Embryo, Mammalian
  • Gene Expression / drug effects
  • Gene Expression / physiology
  • Granulocyte Colony-Stimulating Factor / therapeutic use*
  • Green Fluorescent Proteins
  • Homovanillic Acid / metabolism
  • Immunohistochemistry / methods
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Mice, Transgenic
  • Neurons / drug effects
  • Neurons / metabolism
  • Neuroprotective Agents / therapeutic use*
  • Parkinsonian Disorders / chemically induced
  • Parkinsonian Disorders / prevention & control*
  • RNA, Messenger / metabolism
  • Rats
  • Rats, Wistar
  • Receptors, Granulocyte Colony-Stimulating Factor / genetics
  • Receptors, Granulocyte Colony-Stimulating Factor / metabolism
  • Reverse Transcriptase Polymerase Chain Reaction / methods
  • Transfection / methods
  • Tyrosine 3-Monooxygenase / metabolism

Substances

  • Neuroprotective Agents
  • RNA, Messenger
  • Receptors, Granulocyte Colony-Stimulating Factor
  • 3,4-Dihydroxyphenylacetic Acid
  • Granulocyte Colony-Stimulating Factor
  • Green Fluorescent Proteins
  • 1-Methyl-4-phenyl-1,2,3,6-tetrahydropyridine
  • Tyrosine 3-Monooxygenase
  • Dopamine
  • Homovanillic Acid