Highly efficient regulation of gene expression by tetracycline in a replication-defective herpes simplex viral vector

Mol Ther. 2006 Jun;13(6):1133-41. doi: 10.1016/j.ymthe.2006.01.009. Epub 2006 Mar 29.

Abstract

Employing the tetracycline repressor tetR and the wild-type hCMV major immediate-early promoter, we have developed a highly sensitive tetracycline-inducible transcription switch in mammalian cells (T-REx; Invitrogen, Carlsbad, CA, USA). In view of the previous difficulty in achieving regulatable gene expression in recombinant HSV vector systems, we constructed a T-REx-encoding replication-defective HSV-1 recombinant, QR9TO-lacZ, that encodes two copies of the tetR gene controlled by the HSV-1 immediate-early ICP0 promoter and a reporter, the LacZ gene, under the control of the tetO-bearing hCMV major immediate-early promoter. Infection of cells, such as Vero, PC12, and NGF-differentiated PC12 cells, with QR9TO-lacZ led to 300- to 1000-fold tetracycline-regulated gene expression. Moreover, the expression of the LacZ gene by QR9TO-lacZ can be finely controlled by tetracycline in a dose-dependent fashion. Efficiently regulated gene expression can also be achieved in vivo following intracerebral and footpad inoculations in mice. The demonstrated capability of T-REx for achieving high levels of sensitively regulated gene expression in the context of the HSV-1 genome will significantly expand the utility of HSV-based vector systems for studying gene function in the nervous system and delivering regulated gene expression in therapeutic applications, particularly in the treatment of CNS diseases.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Bacterial Proteins / genetics
  • Carrier Proteins / genetics
  • Chlorocebus aethiops
  • DNA-Binding Proteins / genetics
  • Epidermal Growth Factor / pharmacology
  • Female
  • Gene Expression Regulation, Viral / drug effects*
  • Genetic Vectors / genetics*
  • Herpesvirus 1, Human / drug effects
  • Herpesvirus 1, Human / genetics*
  • Mice
  • Mice, Inbred Strains
  • Nerve Growth Factor / pharmacology
  • PC12 Cells / drug effects
  • PC12 Cells / virology
  • Promoter Regions, Genetic
  • Rats
  • Repressor Proteins / genetics
  • Tetracycline / pharmacology*
  • Toxicity Tests
  • Vero Cells / drug effects
  • Vero Cells / virology
  • Viral Proteins / genetics
  • Virus Replication / drug effects
  • Virus Replication / physiology*
  • beta-Galactosidase / drug effects
  • beta-Galactosidase / genetics
  • beta-Galactosidase / metabolism

Substances

  • Bacterial Proteins
  • Carrier Proteins
  • DNA-Binding Proteins
  • Repressor Proteins
  • Tet O resistance protein, Bacteria
  • Viral Proteins
  • tetracycline resistance-encoding transposon repressor protein
  • UL9 protein, Human herpesvirus 1
  • Epidermal Growth Factor
  • Nerve Growth Factor
  • beta-Galactosidase
  • Tetracycline