Granulocyte colony-stimulating factor corrects the neutropenia associated with glycogen storage disease type Ib

Leukemia. 1991 Apr;5(4):347-9.

Abstract

A young woman with glycogen storage disease, type Ib, and chronic neutropenia had severe recurrent infections. In a life-threatening situation, treatment with granulocyte colony-stimulating factor (G-CSF) resulted in the prompt correction of neutropenia. Subsequently, daily G-CSF therapy has allowed the maintenance of a normal neutrophil count and marked clinical improvement over a period of 18 months. The spectrum of neutropenic conditions which are responsive to G-CSF should include this inherited metabolic disorder.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Female
  • Glycogen Storage Disease Type I / complications*
  • Granulocyte Colony-Stimulating Factor / therapeutic use*
  • Humans
  • Neutropenia / drug therapy*
  • Neutropenia / etiology
  • Recombinant Proteins / therapeutic use

Substances

  • Recombinant Proteins
  • Granulocyte Colony-Stimulating Factor