Antiangiogenic gene therapy with systemically administered sFlt-1 plasmid DNA in engineered gelatin-based nanovectors

Cancer Gene Ther. 2007 May;14(5):488-98. doi: 10.1038/sj.cgt.7701041. Epub 2007 Mar 16.

Abstract

This study examined the potential of engineered gelatin-based nanoparticulate vectors for systemic delivery of therapeutic genes to human solid tumor xenografts in vivo. Plasmid DNA encoding for the soluble form of the extracellular domain of vascular endothelial growth factor receptor-1 (VEGF-R1 or sFlt-1) was encapsulated in the control and poly(ethylene glycol) (PEG)-modified gelatin-based nanoparticles. When the plasmid DNA was delivered in PEG-modified thiolated gelatin nanoparticles, highest levels of sFlt-1 expression was observed in vitro in MDA-MB-435 human breast adenocarcinoma cell line. In addition, upon intravenous administration in female Nu/Nu mice bearing orthotopic MDA-MB-435 breast adenocarcinoma xenografts, efficient in vivo expression of sFlt-1 plasmid DNA was confirmed quantitatively by enzyme-linked immunosorbent assay and qualitatively by Western blot analysis. The expressed sFlt-1 was therapeutically active as shown by suppression of tumor growth and microvessel density measurements. The results of this study show that PEG-modified gelatin-based nanovectors can serve as a safe and effective systemically administered gene delivery vehicle for solid tumor.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Adenocarcinoma / blood supply
  • Adenocarcinoma / chemistry
  • Adenocarcinoma / therapy
  • Animals
  • Breast Neoplasms / blood supply
  • Breast Neoplasms / chemistry
  • Breast Neoplasms / therapy
  • Capsules / administration & dosage
  • Capsules / chemistry
  • Cell Line, Tumor
  • DNA / administration & dosage
  • DNA / chemistry
  • Female
  • Gelatin / chemistry
  • Genetic Therapy*
  • Genetic Vectors* / administration & dosage
  • Genetic Vectors* / chemistry
  • Humans
  • Mice
  • Mice, Inbred Strains
  • Nanoparticles* / administration & dosage
  • Nanoparticles* / chemistry
  • Neovascularization, Pathologic / therapy*
  • Plasmids / administration & dosage
  • Plasmids / chemistry
  • Polyethylene Glycols / chemistry
  • Vascular Endothelial Growth Factor Receptor-1 / analysis
  • Vascular Endothelial Growth Factor Receptor-1 / genetics*
  • Xenograft Model Antitumor Assays

Substances

  • Capsules
  • Polyethylene Glycols
  • Gelatin
  • DNA
  • Vascular Endothelial Growth Factor Receptor-1