Enhanced gene transfer into brain capillary endothelial cells using Antp-modified DNA-loaded nanoparticles

J Biomed Sci. 2007 Sep;14(5):595-605. doi: 10.1007/s11373-007-9171-5. Epub 2007 Apr 20.

Abstract

Brain capillary endothelial cells (BCECs) have been considered as one of the primary targets for cerebral gene therapy. However, the cells, well-known for their poor function of endocytosis, are difficult to be transfected by general non-viral vectors. The aim of this study was to enhance the efficiency of transfection and expression in BCECs of DNA/polymer nanoparticles with the modification of membrane-penetrating peptide, Antennapedia peptide (Antp) polyethylenimine (PEI) and polyamidoamine (PAMAM) were chosen to prepare Antp-modified DNA-loaded nanoparticles with a complex coacervation technique. After a 20-min transfection, the efficiency, in terms of transfection and expression, of DNA/PEI NP or DNA/PAMAM NP was enhanced significantly with the modification of Antp. After a 3-h transfection of DNA/Antp/PEI NP, there was no difference in cellular uptake but an enhancement in gene expression, compared to DNA/PEI NP alone. However, both the transfection and expression efficiency of DNA/PAMAM NP were enhanced using Antp. These observations suggest that Antp can increase the membrane-penetrating ability of DNA-loaded nanoparticles, which can be employed as novel non-viral gene vectors.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antennapedia Homeodomain Protein / chemistry
  • Brain / blood supply*
  • Capillaries / cytology
  • DNA / chemistry
  • Dendrimers
  • Endothelium, Vascular / chemistry
  • Endothelium, Vascular / metabolism*
  • Gene Expression
  • Genetic Therapy*
  • Green Fluorescent Proteins / analysis
  • Green Fluorescent Proteins / genetics
  • Mice
  • Mice, Inbred BALB C
  • Nanoparticles / chemistry*
  • Peptides / chemistry
  • Polyamines / chemistry
  • Polyethyleneimine / chemistry
  • Transfection / methods*

Substances

  • Antennapedia Homeodomain Protein
  • Dendrimers
  • PAMAM Starburst
  • Peptides
  • Polyamines
  • Green Fluorescent Proteins
  • Polyethyleneimine
  • DNA