CINRG pilot trial of oxatomide in steroid-naïve Duchenne muscular dystrophy

Eur J Paediatr Neurol. 2007 Nov;11(6):337-40. doi: 10.1016/j.ejpn.2007.02.009. Epub 2007 Apr 24.

Abstract

The authors report a pilot open-label two-center therapeutic trial of oxatomide in 14 steroid-naive DMD boys aged 5-10 years. Comparison of linear evolutions between 3 months medication-free lead-in periods and 6 months treatment periods showed no significant differences in quantitative (QMT) and manual (MMT) measurements of muscle strength and timed functional tests. A modest mitigation of strength deterioration over time cannot be excluded.

Publication types

  • Controlled Clinical Trial
  • Multicenter Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child
  • Child, Preschool
  • Female
  • Follow-Up Studies
  • Histamine H1 Antagonists / therapeutic use*
  • Humans
  • Linear Models
  • Male
  • Muscle Strength / drug effects
  • Muscular Dystrophy, Duchenne / drug therapy*
  • Pilot Projects
  • Piperazines / therapeutic use*
  • Time Factors
  • Treatment Outcome

Substances

  • Histamine H1 Antagonists
  • Piperazines
  • oxatomide