Pseudodominant Friedreich's ataxia with phenotypic heterogeneity

Acta Neurol Scand. 2007 May;115(5):364-6. doi: 10.1111/j.1600-0404.2007.00734.x.

Abstract

Objective: A family with a clinically heterogeneous progressive ataxia in two generations is presented.

Methods: Having eliminated mutations within the known dominant spinocerebellar ataxia genes, the family was investigated for expansion at the Friedreich's gene.

Results: The affected members (father, son and daughter) were homozygous for the mutation at the Friedreich's gene, while the unaffected (the mother and her sister) were heterozygous.

Conclusion: This pseudodominant form of Friedreich's ataxia should be considered in families with an apparently autosomal dominant progressive ataxia in conjunction with sensory neuropathy and pyramidal signs.

MeSH terms

  • Adult
  • Child
  • Child, Preschool
  • Family Health
  • Female
  • Friedreich Ataxia / genetics*
  • Genes, Dominant*
  • Genetic Heterogeneity*
  • Heterozygote
  • Homozygote
  • Humans
  • Male
  • Pedigree
  • Phenotype