Reversion mutations in patients with leukocyte adhesion deficiency type-1 (LAD-1)

Blood. 2008 Jan 1;111(1):209-18. doi: 10.1182/blood-2007-04-082552. Epub 2007 Sep 17.

Abstract

Leukocyte adhesion deficiency type-1 (LAD-1) is an autosomal recessive immunodeficiency caused by mutations in the beta2 integrin, CD18, that impair CD11/CD18 heterodimer surface expression and/or function. Absence of functional CD11/CD18 integrins on leukocytes, particularly neutrophils, leads to their incapacity to adhere to the endothelium and migrate to sites of infection. We studied 3 LAD-1 patients with markedly diminished neutrophil CD18 expression, each of whom had a small population of lymphocytes with normal CD18 expression (CD18(+)). These CD18(+) lymphocytes were predominantly cytotoxic T cells, with a memory/effector phenotype. Microsatellite analyses proved patient origin of these cells. Sequencing of T-cell subsets showed that in each patient one CD18 allele had undergone further mutation. Interestingly, all 3 patients were young adults with inflammatory bowel disease. Somatic reversions of inherited mutations in primary T-cell immunodeficiencies are typically associated with milder clinical phenotypes. We hypothesize that these somatic revertant CD18(+) cytotoxic T lymphocytes (CTLs) may have altered immune regulation. The discovery of 3 cases of reversion mutations in LAD-1 at one center suggests that this may be a relatively common event in this rare disease.

Publication types

  • Research Support, N.I.H., Intramural

MeSH terms

  • Adult
  • CD18 Antigens / genetics*
  • CD8 Antigens / genetics
  • Female
  • Genes, Recessive
  • Humans
  • Immunologic Memory / genetics
  • Immunophenotyping
  • Integrin alpha Chains / genetics
  • Leukocyte-Adhesion Deficiency Syndrome / genetics*
  • Leukocyte-Adhesion Deficiency Syndrome / immunology*
  • Male
  • Mosaicism*
  • Mutation
  • Neutropenia / genetics
  • Superantigens / genetics
  • T-Lymphocytes, Cytotoxic / physiology*

Substances

  • CD18 Antigens
  • CD8 Antigens
  • Integrin alpha Chains
  • Superantigens