Progress and problems when considering gene therapy for GSD-II

Acta Myol. 2007 Jul;26(1):49-52.

Authors

A Kiang¹, A Amalfitano

Affiliation

¹ Department of Microbiology and Molecular Genetics, Michigan State University, East Lansing, MI 48824, USA.

PMID: 17915570
PMCID: PMC2949318

No abstract available

Publication types

Review

MeSH terms

Genetic Therapy / trends*
Glycogen Storage Disease Type II / enzymology
Glycogen Storage Disease Type II / genetics*
Humans
Receptors, Cell Surface / genetics
alpha-Glucosidases / genetics

Substances

Receptors, Cell Surface
GAA protein, human
alpha-Glucosidases